FDA approves Roche, PTC drug for spinal muscular atrophy
The Food and Drug Administration has approved the latest entrant into the market for drugs to treat spinal muscular atrophy. South Plainfield, New Jersey-based PTC...
Tag : spinal
Biogen to launch Phase IV study of spinal muscular atrophy drug in post-gene therapy patients
While a gene therapy approved last year for spinal muscular atrophy has made a significant difference in the lives of most patients, some experience less-than-optimal...